I am so happy that Translarna has been approved for the boys with Duchenne Muscular Dystrophy. One mum equated it to winning the lottery – only better.
Children’s health should not be a lottery…and the fight continues for Spinraza.
Join the march to Leinster House on SMA Ireland Day of Action on Spinraza – World Rare Disease Day this Thursday, Feb 28th. More info: https://bit.ly/2tE2U2F
